Stagione 1
Dom on having Gene Therapy for Haemophilia A
Gene Therapy: 'Ask me Anything' with Dr Michiel Coppens
Steve on having gene therapy for haemophilia A
Dom shares his experience of receiving gene therapy treatment for haemophilia A. He talks about his life with haemophilia, before and after gene therapy. For Dom, the gene therapy wasn't a success, however he is still very positive about his experience. As of May 2026, gene therapy for haemophilia is currently only available in Australia through clinical trials. Gene therapy for haemophilia B is in the process of being evaluated by the Australian Government for funding to become available for Australians and we look forward to the outcome. Dom is Australian and received gene therapy as part of a clinical trial.
Chaired by Dr Stephanie P’ng and led by questions from the community, Dr Michiel Coppens explains what gene therapy is, how it works, and how it can be used to treat people with haemophilia. Dr Coppens draws on his extensive knowledge of haemophilia and experience in gene therapy – he dosed the first Dutch patient with gene therapy back in 2015 – to provide answers that are both thorough and easy to understand. This interview was recorded on 14 May 2024.
Steve shares his experience having gene therapy for severe haemophilia A – and how it has changed his life. As of May 2026, gene therapy for haemophilia is currently only available in Australia through clinical trials. Gene therapy for haemophilia B is in the process of being evaluated by the Australian Government for funding to become available for Australians and we look forward to the outcome.
HFA met with Prof Cedric Hermans during the Australian Bleeding Disorders Conference 2025. Prof Cedric is from Saint-Luc University Hospital, Belgium, and spoke with us on a variety of topics, including: The changing landscape of treatment options for haemophilia and other bleeding disorders Women and girls with bleeding disorders The importance of diagnosis